Executive Director, Global Medical Lead – LC-FAOD, MPS VII, MPS IIIA
Job Description:
• Serve as Global Medical Lead for LC-FAOD (Dojolvi) and the MPS programs, including MPS VII (Mepsevii) and MPS IIIA (UX111)
• Lead the Global Medical Sub Teams (GMSTs), setting the strategy for the programs, ensuring cross regional alignment, and driving timely execution of annual medical plan
• Guide and oversee prelaunch planning, launch execution, and postlaunch optimization across the globe
• Serve as the strategic medical leader on the Program Core Team and related sub-teams, shaping development, commercialization, and lifecycle strategies. Work decisively to overcome challenges and drive program priorities forward
• Own, develop, and update the Integrated Evidence Generation Plans (IEPs) for all assigned programs ensuring cross functional alignment to address global/regional evidence gaps
• Oversee global Real World Evidence initiatives, including ISTs and collaborative research that inform clinical decision making and regulatory objectives.
• Accountable as the medical affairs lead for Disease Monitoring Programs for LC-FAOD and MPSs, providing strategic medical leadership on all aspects of the study and accountable for leading data generation and publication activities aligned to the IEP
• Lead advisory boards, steering committees, and investigator meetings to gather key insights that inform program strategy and activities
• Provide deep disease area and product expertise, ensuring accurate and consistent communication of clinical and scientific data
• Direct global publication strategy and congress planning activities, ensuring timely, high-impact dissemination of data and other education initiatives
• Lead training and provide strategic guidance and tools to regional medical affairs teams to ensure launch readiness and consistent scientific exchange
• Build and maintain relationships with global KOLs, academic centers of excellence, scientific societies and advocacy groups to inform strategy and amplify scientific reach
• Monitor competitors and landscape changes, translating insights into strategic actions.
Requirements:
• Medical Doctor (MD) required. MD, PhD strongly preferred. 7+ years of combined industry and academic experience preferred. Board Certification or equivalent in Clinical/Biochemical Genetics or Neurology preferred
• Proven expertise in the management of patients with inherited metabolic and/or neurodegenerative rare diseases
• Recognized scientific authority with the ability to engage in advanced scientific and clinical discussions with both internal and external experts
• Proven leadership skills including a passion for collaboration and understanding all stakeholder perspectives to drive alignment and decision-making
• High aptitude for attention to detail, commitment to high-quality work, and a sense of passion and urgency to achieve goals and improve the lives of patients
• Proven ability to take initiative and drive successful execution of complex projects
• Highly analytical and strategic thinker with the ability to identify interdependencies, consider medical implications, and understand the broader goals of a program and the organization
• Excellent communication skills, with the ability to effectively articulate scientific and strategic concepts in both written documents and verbal presentations
• Demonstrated success leading cross functional or multidisciplinary teams, ideally in both academia and biotech
• Willingness and ability to travel up to 15%, including domestic and international engagements
Benefits:
• Generous vacation time and public holidays observed by the company
• Volunteer days
• Long term incentive and Employee stock purchase plans or equivalent offerings
• Employee wellbeing benefits
• Fitness reimbursement
• Tuition sponsoring
• Professional development plans
Apply Now
Apply Now
• Serve as Global Medical Lead for LC-FAOD (Dojolvi) and the MPS programs, including MPS VII (Mepsevii) and MPS IIIA (UX111)
• Lead the Global Medical Sub Teams (GMSTs), setting the strategy for the programs, ensuring cross regional alignment, and driving timely execution of annual medical plan
• Guide and oversee prelaunch planning, launch execution, and postlaunch optimization across the globe
• Serve as the strategic medical leader on the Program Core Team and related sub-teams, shaping development, commercialization, and lifecycle strategies. Work decisively to overcome challenges and drive program priorities forward
• Own, develop, and update the Integrated Evidence Generation Plans (IEPs) for all assigned programs ensuring cross functional alignment to address global/regional evidence gaps
• Oversee global Real World Evidence initiatives, including ISTs and collaborative research that inform clinical decision making and regulatory objectives.
• Accountable as the medical affairs lead for Disease Monitoring Programs for LC-FAOD and MPSs, providing strategic medical leadership on all aspects of the study and accountable for leading data generation and publication activities aligned to the IEP
• Lead advisory boards, steering committees, and investigator meetings to gather key insights that inform program strategy and activities
• Provide deep disease area and product expertise, ensuring accurate and consistent communication of clinical and scientific data
• Direct global publication strategy and congress planning activities, ensuring timely, high-impact dissemination of data and other education initiatives
• Lead training and provide strategic guidance and tools to regional medical affairs teams to ensure launch readiness and consistent scientific exchange
• Build and maintain relationships with global KOLs, academic centers of excellence, scientific societies and advocacy groups to inform strategy and amplify scientific reach
• Monitor competitors and landscape changes, translating insights into strategic actions.
Requirements:
• Medical Doctor (MD) required. MD, PhD strongly preferred. 7+ years of combined industry and academic experience preferred. Board Certification or equivalent in Clinical/Biochemical Genetics or Neurology preferred
• Proven expertise in the management of patients with inherited metabolic and/or neurodegenerative rare diseases
• Recognized scientific authority with the ability to engage in advanced scientific and clinical discussions with both internal and external experts
• Proven leadership skills including a passion for collaboration and understanding all stakeholder perspectives to drive alignment and decision-making
• High aptitude for attention to detail, commitment to high-quality work, and a sense of passion and urgency to achieve goals and improve the lives of patients
• Proven ability to take initiative and drive successful execution of complex projects
• Highly analytical and strategic thinker with the ability to identify interdependencies, consider medical implications, and understand the broader goals of a program and the organization
• Excellent communication skills, with the ability to effectively articulate scientific and strategic concepts in both written documents and verbal presentations
• Demonstrated success leading cross functional or multidisciplinary teams, ideally in both academia and biotech
• Willingness and ability to travel up to 15%, including domestic and international engagements
Benefits:
• Generous vacation time and public holidays observed by the company
• Volunteer days
• Long term incentive and Employee stock purchase plans or equivalent offerings
• Employee wellbeing benefits
• Fitness reimbursement
• Tuition sponsoring
• Professional development plans
Apply Now
Apply Now